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Targeted RNA base editing for therapeutic: mechanisms and advances

RNA base editing, which enables RNA base modification through effector proteins guided by targeting systems, is a powerful technology to correct disease-associated point mutations. Although overshadowed by CRISPR-based genome editing, RNA editing has seen rapid development in recent years, with sign...

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Detalles Bibliográficos
Principais autores: Weikai Yan, Xiaocheng Weng
Formato: Artigo
Idioma:Inglês
Publicado: Elsevier 2025-12-01
Series:Pharmaceutical Science Advances
Assuntos:
Acceso en liña:http://www.sciencedirect.com/science/article/pii/S2773216925000273
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