Targeted RNA base editing for therapeutic: mechanisms and advances
RNA base editing, which enables RNA base modification through effector proteins guided by targeting systems, is a powerful technology to correct disease-associated point mutations. Although overshadowed by CRISPR-based genome editing, RNA editing has seen rapid development in recent years, with sign...
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| Principais autores: | , |
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| Formato: | Artigo |
| Idioma: | Inglês |
| Publicado: |
Elsevier
2025-12-01
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| Series: | Pharmaceutical Science Advances |
| Assuntos: | |
| Acceso en liña: | http://www.sciencedirect.com/science/article/pii/S2773216925000273 |
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