PMP22 antisense oligonucleotides reverse Charcot-Marie-Tooth disease type 1A features in rodent models

Por Zhao, Hien Tran, Damle, Sagar, Ikeda-Lee, Karli, Kuntz, Steven, Li, Jian, Mohan, Apoorva, Kim, Aneeza, Hung, Gene, Scheideler, Mark A., Scherer, Steven S., Svaren, John, Swayze, Eric E., Kordasiewicz, Holly B.
Publicado no J Clin Invest (2017)