Simple downstream process based on detergent treatment improves yield and in vivo transduction efficacy of adeno-associated virus vectors

Por Dias Florencio, Gabriella, Precigout, Guillaume, Beley, Cyriaque, Buclez, Pierre-Olivier, Garcia, Luis, Benchaouir, Rachid
Publicado no Mol Ther Methods Clin Dev (2015)

AAV Genome Loss From Dystrophic Mouse Muscles During AAV-U7 snRNA-mediated Exon-skipping Therapy

Por Le Hir, Maëva, Goyenvalle, Aurélie, Peccate, Cécile, Précigout, Guillaume, Davies, Kay E, Voit, Thomas, Garcia, Luis, Lorain, Stéphanie
Publicado em 2013

Dystrophin rescue by trans-splicing: a strategy for DMD genotypes not eligible for exon skipping approaches

Por Lorain, Stéphanie, Peccate, Cécile, Le Hir, Maëva, Griffith, Graziella, Philippi, Susanne, Précigout, Guillaume, Mamchaoui, Kamel, Jollet, Arnaud, Voit, Thomas, Garcia, Luis
Publicado em 2013

Repair of Mybpc3 mRNA by 5′-trans-splicing in a Mouse Model of Hypertrophic Cardiomyopathy

Por Mearini, Giulia, Stimpel, Doreen, Krämer, Elisabeth, Geertz, Birgit, Braren, Ingke, Gedicke-Hornung, Christina, Précigout, Guillaume, Müller, Oliver J, Katus, Hugo A, Eschenhagen, Thomas, Voit, Thomas, Garcia, Luis, Lorain, Stéphanie, Carrier, Lucie
Publicado em 2013

Actin scaffolding by clathrin heavy chain is required for skeletal muscle sarcomere organization

Por Vassilopoulos, Stéphane, Gentil, Christel, Lainé, Jeanne, Buclez, Pierre-Olivier, Franck, Agathe, Ferry, Arnaud, Précigout, Guillaume, Roth, Robyn, Heuser, John E., Brodsky, Frances M., Garcia, Luis, Bonne, Gisèle, Voit, Thomas, Piétri-Rouxel, France, Bitoun, Marc
Publicado em 2014

Rescue of cardiomyopathy through U7snRNA-mediated exon skipping in Mybpc3-targeted knock-in mice

Por Gedicke-Hornung, Christina, Behrens-Gawlik, Verena, Reischmann, Silke, Geertz, Birgit, Stimpel, Doreen, Weinberger, Florian, Schlossarek, Saskia, Précigout, Guillaume, Braren, Ingke, Eschenhagen, Thomas, Mearini, Giulia, Lorain, Stéphanie, Voit, Thomas, Dreyfus, Patrick A, Garcia, Luis, Carrier, Lucie
Publicado em 2013