Antisense-induced exon skipping and synthesis of dystrophin in the mdx mouse

Autor Mann, Christopher J., Honeyman, Kaite, Cheng, Andy J., Ly, Tina, Lloyd, Frances, Fletcher, Sue, Morgan, Jennifer E., Partridge, Terry A., Wilton, Stephen D.
Vydáno 2001

Discovery of serum protein biomarkers in the mdx mouse model and cross-species comparison to Duchenne muscular dystrophy patients

Autor Hathout, Yetrib, Marathi, Ramya L., Rayavarapu, Sree, Zhang, Aiping, Brown, Kristy J., Seol, Haeri, Gordish-Dressman, Heather, Cirak, Sebahattin, Bello, Luca, Nagaraju, Kanneboyina, Partridge, Terry, Hoffman, Eric P., Takeda, Shin'ichi, Mah, Jean K., Henricson, Erik, McDonald, Craig
Vydáno v Hum Mol Genet (2014)

Effects of systemic multiexon skipping with peptide-conjugated morpholinos in the heart of a dog model of Duchenne muscular dystrophy

Autor Echigoya, Yusuke, Nakamura, Akinori, Nagata, Tetsuya, Urasawa, Nobuyuki, Lim, Kenji Rowel Q., Trieu, Nhu, Panesar, Dharminder, Kuraoka, Mutsuki, Moulton, Hong M., Saito, Takashi, Aoki, Yoshitsugu, Iversen, Patrick, Sazani, Peter, Kole, Ryszard, Maruyama, Rika, Partridge, Terry, Takeda, Shin’ichi, Yokota, Toshifumi
Vydáno v Proc Natl Acad Sci U S A (2017)

“Of Mice and Measures”: A Project to Improve How We Advance Duchenne Muscular Dystrophy Therapies to the Clinic: First Workshop Report: Examining current findings and opportunities...

Autor Gordish-Dressman, Heather, Willmann, Raffaella, Dalle Pazze, Laura, Kreibich, Arati, van Putten, Maaike, Heydemann, Ahlke, Bogdanik, Laurent, Lutz, Cathleen, Davies, Kay, Demonbreun, Alexis R., Duan, Dongsheng, Elsey, David, Fukada, So-ichiro, Girgenrath, Mahasweta, Patrick Gonzalez, J., Grounds, Miranda D., Nichols, Andy, Partridge, Terry, Passini, Marco, Sanarica, Francesca, Schnell, Frederick J., Wells, Dominic J., Yokota, Toshifumi, Young, Courtney S., Zhong, Zhong, Spurney, Christopher, Spencer, Melissa, De Luca, Annamaria, Nagaraju, Kanneboyina, Aartsma-Rus, Annemieke
Vydáno v J Neuromuscul Dis (2018)