Alpharetroviral Vector-mediated Gene Therapy for X-CGD: Functional Correction and Lack of Aberrant Splicing

Por Kaufmann, Kerstin B., Brendel, Christian, Suerth, Julia D., Mueller-Kuller, Uta, Chen-Wichmann, Linping, Schwäble, Joachim, Pahujani, Shweta, Kunkel, Hana, Schambach, Axel, Baum, Christopher, Grez, Manuel
Publicado em 2013

Safer, Silencing-Resistant Lentiviral Vectors: Optimization of the Ubiquitous Chromatin-Opening Element through Elimination of Aberrant Splicing

Por Knight, Sean, Zhang, Fang, Mueller-Kuller, Uta, Bokhoven, Marieke, Gupta, Abhinav, Broughton, Thomas, Sha, Sha, Antoniou, Michael N., Brendel, Christian, Grez, Manuel, Thrasher, Adrian J., Collins, Mary, Takeuchi, Yasuhiro
Publicado em 2012