Reply to Letter to the Editor

av Mendell, Jerry R.
I publikationen Mol Ther (2017)

Duchenne muscular dystrophy: CRISPR/Cas9 treatment

av Mendell, Jerry R, Rodino-Klapac, Louise R
I publikationen Cell Res (2016)

Casein Kinase 1 alpha associates with the tau-bearing lesions of inclusion body myositis

av Kannanayakal, Theresa J., Mendell, Jerry R., Kuret, Jeff
Publicerad 2007

The Congenital Muscular Dystrophies: Recent Advances and Molecular Insights

av Mendell, Jerry R., Boué, Daniel R., Martin, Paul T.
Publicerad 2006

Emerging Drugs for Duchenne Muscular Dystrophy

av Malik, Vinod, Rodino-Klapac, Louise, Mendell, Jerry R.
Publicerad 2012

Could gene therapy be the future for muscular dystrophy?

av Haidet, Amanda M, Mendell, Jerry R, Kaspar, Brian K
Publicerad 2010

Molecular Therapeutic Strategies Targeting Duchenne Muscular Dystrophy

av Mendell, Jerry R., Rodino-Klapac, Louise R., Malik, Vinod
Publicerad 2010

Gene Therapy for Muscular Dystrophy: Moving the Field Forward

av Al-Zaidy, Samiah, Rodino-Klapac, Louise, Mendell, Jerry R
I publikationen Pediatr Neurol (2014)

Update on the Treatment of Duchenne Muscular Dystrophy

av Rodino-Klapac, Louise R., Mendell, Jerry R., Sahenk, Zarife
I publikationen Curr Neurol Neurosci Rep (2013)

Evaluatíon and treatment of myopathies /

av Griggs, Robert C., Mendell, Jerry R., Miller, Robert G.
Publicerad 1995.

Aminoglycoside-induced mutation suppression (stop codon readthrough) as a therapeutic strategy for Duchenne muscular dystrophy

av Malik, Vinod, Rodino-Klapac, Louise R., Viollet, Laurence, Mendell, Jerry R.
Publicerad 2010

MicroRNA-29 overexpression by adeno-associated virus suppresses fibrosis and restores muscle function in combination with micro-dystrophin

av Heller, Kristin N., Mendell, Joshua T., Mendell, Jerry R., Rodino-Klapac, Louise R.
I publikationen JCI Insight (2017)

A Roadmap to Newborn Screening for Duchenne Muscular Dystrophy

av Al-Zaidy, Samiah A., Lloyd-Puryear, Michele, Kennedy, Annie, Lopez, Veronica, Mendell, Jerry R.
I publikationen Int J Neonatal Screen (2017)

Follistatin Gene Therapy Improves Ambulation in Becker Muscular Dystrophy

av Al-Zaidy, Samiah A., Sahenk, Zarife, Rodino-Klapac, Louise R., Kaspar, Brian, Mendell, Jerry R.
I publikationen J Neuromuscul Dis (2015)

Systemic AAV-Mediated β-Sarcoglycan Delivery Targeting Cardiac and Skeletal Muscle Ameliorates Histological and Functional Deficits in LGMD2E Mice

av Pozsgai, Eric R., Griffin, Danielle A., Heller, Kristin N., Mendell, Jerry R., Rodino-Klapac, Louise R.
I publikationen Mol Ther (2017)

Rapid Direct Sequence Analysis of the Dystrophin Gene

av Flanigan, Kevin M., Niederhausern, Andrew von, Dunn, Diane M., Alder, Jonathan, Mendell, Jerry R., Weiss, Robert B.
Publicerad 2003

INHIBITION OF MYOSTATIN WITH EMPHASIS ON FOLLISTATIN AS A THERAPY FOR MUSCLE DISEASE

av RODINO-KLAPAC, LOUISE R., HAIDET, AMANDA M., KOTA, JANAIAH, HANDY, CHALONDA, KASPAR, BRIAN K., MENDELL, JERRY R.
Publicerad 2009

Long-Term Pulmonary Function in Duchenne Muscular Dystrophy: Comparison of Eteplirsen-Treated Patients to Natural History

av Kinane, T. Bernard, Mayer, Oscar H., Duda, Petra W., Lowes, Linda P., Moody, Stephanie L., Mendell, Jerry R.
I publikationen J Neuromuscul Dis (2018)

Anti-Dystrophin T Cell Responses in Duchenne Muscular Dystrophy: Prevalence and a Glucocorticoid Treatment Effect

av Flanigan, Kevin M., Campbell, Katie, Viollet, Laurence, Wang, Wei, Gomez, Ana Maria, Walker, Christopher M., Mendell, Jerry R.
Publicerad 2013

Utility of Cystatin C to monitor renal function in Duchenne muscular dystrophy

av Viollet, Laurence, Gailey, Susan, Thornton, David J., Friedman, Neil R., Flanigan, Kevin M., Mahan, John D., Mendell, Jerry R.
Publicerad 2009