Reply to Letter to the Editor

door Mendell, Jerry R.
Gepubliceerd in Mol Ther (2017)

Duchenne muscular dystrophy: CRISPR/Cas9 treatment

door Mendell, Jerry R, Rodino-Klapac, Louise R
Gepubliceerd in Cell Res (2016)

Casein Kinase 1 alpha associates with the tau-bearing lesions of inclusion body myositis

door Kannanayakal, Theresa J., Mendell, Jerry R., Kuret, Jeff
Gepubliceerd in 2007

The Congenital Muscular Dystrophies: Recent Advances and Molecular Insights

door Mendell, Jerry R., Boué, Daniel R., Martin, Paul T.
Gepubliceerd in 2006

Emerging Drugs for Duchenne Muscular Dystrophy

door Malik, Vinod, Rodino-Klapac, Louise, Mendell, Jerry R.
Gepubliceerd in 2012

Could gene therapy be the future for muscular dystrophy?

door Haidet, Amanda M, Mendell, Jerry R, Kaspar, Brian K
Gepubliceerd in 2010

Molecular Therapeutic Strategies Targeting Duchenne Muscular Dystrophy

door Mendell, Jerry R., Rodino-Klapac, Louise R., Malik, Vinod
Gepubliceerd in 2010

Gene Therapy for Muscular Dystrophy: Moving the Field Forward

door Al-Zaidy, Samiah, Rodino-Klapac, Louise, Mendell, Jerry R
Gepubliceerd in Pediatr Neurol (2014)

Update on the Treatment of Duchenne Muscular Dystrophy

door Rodino-Klapac, Louise R., Mendell, Jerry R., Sahenk, Zarife
Gepubliceerd in Curr Neurol Neurosci Rep (2013)

Evaluatíon and treatment of myopathies /

door Griggs, Robert C., Mendell, Jerry R., Miller, Robert G.
Gepubliceerd in 1995.

Aminoglycoside-induced mutation suppression (stop codon readthrough) as a therapeutic strategy for Duchenne muscular dystrophy

door Malik, Vinod, Rodino-Klapac, Louise R., Viollet, Laurence, Mendell, Jerry R.
Gepubliceerd in 2010

MicroRNA-29 overexpression by adeno-associated virus suppresses fibrosis and restores muscle function in combination with micro-dystrophin

door Heller, Kristin N., Mendell, Joshua T., Mendell, Jerry R., Rodino-Klapac, Louise R.
Gepubliceerd in JCI Insight (2017)

A Roadmap to Newborn Screening for Duchenne Muscular Dystrophy

door Al-Zaidy, Samiah A., Lloyd-Puryear, Michele, Kennedy, Annie, Lopez, Veronica, Mendell, Jerry R.
Gepubliceerd in Int J Neonatal Screen (2017)

Follistatin Gene Therapy Improves Ambulation in Becker Muscular Dystrophy

door Al-Zaidy, Samiah A., Sahenk, Zarife, Rodino-Klapac, Louise R., Kaspar, Brian, Mendell, Jerry R.
Gepubliceerd in J Neuromuscul Dis (2015)

Systemic AAV-Mediated β-Sarcoglycan Delivery Targeting Cardiac and Skeletal Muscle Ameliorates Histological and Functional Deficits in LGMD2E Mice

door Pozsgai, Eric R., Griffin, Danielle A., Heller, Kristin N., Mendell, Jerry R., Rodino-Klapac, Louise R.
Gepubliceerd in Mol Ther (2017)

Rapid Direct Sequence Analysis of the Dystrophin Gene

door Flanigan, Kevin M., Niederhausern, Andrew von, Dunn, Diane M., Alder, Jonathan, Mendell, Jerry R., Weiss, Robert B.
Gepubliceerd in 2003

INHIBITION OF MYOSTATIN WITH EMPHASIS ON FOLLISTATIN AS A THERAPY FOR MUSCLE DISEASE

door RODINO-KLAPAC, LOUISE R., HAIDET, AMANDA M., KOTA, JANAIAH, HANDY, CHALONDA, KASPAR, BRIAN K., MENDELL, JERRY R.
Gepubliceerd in 2009

Long-Term Pulmonary Function in Duchenne Muscular Dystrophy: Comparison of Eteplirsen-Treated Patients to Natural History

door Kinane, T. Bernard, Mayer, Oscar H., Duda, Petra W., Lowes, Linda P., Moody, Stephanie L., Mendell, Jerry R.
Gepubliceerd in J Neuromuscul Dis (2018)

Anti-Dystrophin T Cell Responses in Duchenne Muscular Dystrophy: Prevalence and a Glucocorticoid Treatment Effect

door Flanigan, Kevin M., Campbell, Katie, Viollet, Laurence, Wang, Wei, Gomez, Ana Maria, Walker, Christopher M., Mendell, Jerry R.
Gepubliceerd in 2013

Utility of Cystatin C to monitor renal function in Duchenne muscular dystrophy

door Viollet, Laurence, Gailey, Susan, Thornton, David J., Friedman, Neil R., Flanigan, Kevin M., Mahan, John D., Mendell, Jerry R.
Gepubliceerd in 2009