Reply to Letter to the Editor

द्वारा Mendell, Jerry R.
में प्रकाशित Mol Ther (2017)

Duchenne muscular dystrophy: CRISPR/Cas9 treatment

द्वारा Mendell, Jerry R, Rodino-Klapac, Louise R
में प्रकाशित Cell Res (2016)

Casein Kinase 1 alpha associates with the tau-bearing lesions of inclusion body myositis

द्वारा Kannanayakal, Theresa J., Mendell, Jerry R., Kuret, Jeff
प्रकाशित 2007

The Congenital Muscular Dystrophies: Recent Advances and Molecular Insights

द्वारा Mendell, Jerry R., Boué, Daniel R., Martin, Paul T.
प्रकाशित 2006

Emerging Drugs for Duchenne Muscular Dystrophy

द्वारा Malik, Vinod, Rodino-Klapac, Louise, Mendell, Jerry R.
प्रकाशित 2012

Could gene therapy be the future for muscular dystrophy?

द्वारा Haidet, Amanda M, Mendell, Jerry R, Kaspar, Brian K
प्रकाशित 2010

Molecular Therapeutic Strategies Targeting Duchenne Muscular Dystrophy

द्वारा Mendell, Jerry R., Rodino-Klapac, Louise R., Malik, Vinod
प्रकाशित 2010

Gene Therapy for Muscular Dystrophy: Moving the Field Forward

द्वारा Al-Zaidy, Samiah, Rodino-Klapac, Louise, Mendell, Jerry R
में प्रकाशित Pediatr Neurol (2014)

Update on the Treatment of Duchenne Muscular Dystrophy

द्वारा Rodino-Klapac, Louise R., Mendell, Jerry R., Sahenk, Zarife
में प्रकाशित Curr Neurol Neurosci Rep (2013)

Evaluatíon and treatment of myopathies /

द्वारा Griggs, Robert C., Mendell, Jerry R., Miller, Robert G.
प्रकाशित 1995.

Aminoglycoside-induced mutation suppression (stop codon readthrough) as a therapeutic strategy for Duchenne muscular dystrophy

द्वारा Malik, Vinod, Rodino-Klapac, Louise R., Viollet, Laurence, Mendell, Jerry R.
प्रकाशित 2010

MicroRNA-29 overexpression by adeno-associated virus suppresses fibrosis and restores muscle function in combination with micro-dystrophin

द्वारा Heller, Kristin N., Mendell, Joshua T., Mendell, Jerry R., Rodino-Klapac, Louise R.
में प्रकाशित JCI Insight (2017)

A Roadmap to Newborn Screening for Duchenne Muscular Dystrophy

द्वारा Al-Zaidy, Samiah A., Lloyd-Puryear, Michele, Kennedy, Annie, Lopez, Veronica, Mendell, Jerry R.
में प्रकाशित Int J Neonatal Screen (2017)

Follistatin Gene Therapy Improves Ambulation in Becker Muscular Dystrophy

द्वारा Al-Zaidy, Samiah A., Sahenk, Zarife, Rodino-Klapac, Louise R., Kaspar, Brian, Mendell, Jerry R.
में प्रकाशित J Neuromuscul Dis (2015)

Systemic AAV-Mediated β-Sarcoglycan Delivery Targeting Cardiac and Skeletal Muscle Ameliorates Histological and Functional Deficits in LGMD2E Mice

द्वारा Pozsgai, Eric R., Griffin, Danielle A., Heller, Kristin N., Mendell, Jerry R., Rodino-Klapac, Louise R.
में प्रकाशित Mol Ther (2017)

Rapid Direct Sequence Analysis of the Dystrophin Gene

द्वारा Flanigan, Kevin M., Niederhausern, Andrew von, Dunn, Diane M., Alder, Jonathan, Mendell, Jerry R., Weiss, Robert B.
प्रकाशित 2003

INHIBITION OF MYOSTATIN WITH EMPHASIS ON FOLLISTATIN AS A THERAPY FOR MUSCLE DISEASE

द्वारा RODINO-KLAPAC, LOUISE R., HAIDET, AMANDA M., KOTA, JANAIAH, HANDY, CHALONDA, KASPAR, BRIAN K., MENDELL, JERRY R.
प्रकाशित 2009

Long-Term Pulmonary Function in Duchenne Muscular Dystrophy: Comparison of Eteplirsen-Treated Patients to Natural History

द्वारा Kinane, T. Bernard, Mayer, Oscar H., Duda, Petra W., Lowes, Linda P., Moody, Stephanie L., Mendell, Jerry R.
में प्रकाशित J Neuromuscul Dis (2018)

Anti-Dystrophin T Cell Responses in Duchenne Muscular Dystrophy: Prevalence and a Glucocorticoid Treatment Effect

द्वारा Flanigan, Kevin M., Campbell, Katie, Viollet, Laurence, Wang, Wei, Gomez, Ana Maria, Walker, Christopher M., Mendell, Jerry R.
प्रकाशित 2013

Utility of Cystatin C to monitor renal function in Duchenne muscular dystrophy

द्वारा Viollet, Laurence, Gailey, Susan, Thornton, David J., Friedman, Neil R., Flanigan, Kevin M., Mahan, John D., Mendell, Jerry R.
प्रकाशित 2009