Efficient Expression of Igf-1 from Lentiviral Vectors Protects In Vitro but Does Not Mediate Behavioral Recovery of a Parkinsonian Lesion in Rats

af Lu-Nguyen, Ngoc B., Broadstock, Martin, Yáñez-Muñoz, Rafael J.
Udgivet i Hum Gene Ther (2015)

Combination Antisense Treatment for Destructive Exon Skipping of Myostatin and Open Reading Frame Rescue of Dystrophin in Neonatal mdx Mice

af Lu-Nguyen, Ngoc B, Jarmin, Susan A, Saleh, Amer F, Popplewell, Linda, Gait, Michael J, Dickson, George
Udgivet i Mol Ther (2015)

Transgenic Expression of Human Glial Cell Line-Derived Neurotrophic Factor from Integration-Deficient Lentiviral Vectors is Neuroprotective in a Rodent Model of Parkinson's Disease

af Lu-Nguyen, Ngoc B., Broadstock, Martin, Schliesser, Maximilian G., Bartholomae, Cynthia C., von Kalle, Christof, Schmidt, Manfred, Yáñez-Muñoz, Rafael J.
Udgivet 2014

Functional Rescue of Dystrophin Deficiency in Mice Caused by Frameshift Mutations Using Campylobacter jejuni Cas9

af Koo, Taeyoung, Lu-Nguyen, Ngoc B., Malerba, Alberto, Kim, Eunji, Kim, Daesik, Cappellari, Ornella, Cho, Hee-Yeon, Dickson, George, Popplewell, Linda, Kim, Jin-Soo
Udgivet i Mol Ther (2018)