Rapid and Sensitive Assessment of Globin Chains for Gene and Cell Therapy of Hemoglobinopathies

por Loucari, Constantinos C., Patsali, Petros, van Dijk, Thamar B., Stephanou, Coralea, Papasavva, Panayiota, Zanti, Maria, Kurita, Ryo, Nakamura, Yukio, Christou, Soteroulla, Sitarou, Maria, Philipsen, Sjaak, Lederer, Carsten W., Kleanthous, Marina
Publicado en Hum Gene Ther Methods (2018)

Correction of IVS I-110(G>A) β-thalassemia by CRISPR/Cas-and TALEN-mediated disruption of aberrant regulatory elements in human hematopoietic stem and progenitor cells

por Patsali, Petros, Turchiano, Giandomenico, Papasavva, Panayiota, Romito, Marianna, Loucari, Constantinos C., Stephanou, Coralea, Christou, Soteroulla, Sitarou, Maria, Mussolino, Claudio, Cornu, Tatjana I., Antoniou, Michael N., Lederer, Carsten W., Cathomen, Toni, Kleanthous, Marina
Publicado en Haematologica (2019)