Post Hoc Analysis of Nutritional Status in Patients with Transthyretin Familial Amyloid Polyneuropathy: Impact of Tafamidis

Autor Suhr, Ole B., Conceição, Isabel M., Karayal, Onur N., Mandel, Francine S., Huertas, Pedro E., Ericzon, Bo‐Göran
Vydáno v Neurol Ther (2014)

The novel aminoglycoside, ELX-02, permits CTNS(W138X) translational read-through and restores lysosomal cystine efflux in cystinosis

Autor Brasell, Emma J., Chu, Lee Lee, Akpa, Murielle M., Eshkar-Oren, Idit, Alroy, Iris, Corsini, Rachel, Gilfix, Brian M., Yamanaka, Yojiro, Huertas, Pedro, Goodyer, Paul
Vydáno v PLoS One (2019)

Intra-Articular Injections of Platelet-Rich Plasma versus Hyaluronic Acid in the Treatment of Osteoarthritic Knee Pain: A Randomized Clinical Trial in the Context of the Spanish Na...

Autor Montañez-Heredia, Elvira, Irízar, Sofia, Huertas, Pedro J., Otero, Esperanza, del Valle, Marta, Prat, Isidro, Díaz-Gallardo, Macarena S., Perán, Macarena, Marchal, Juan A., Hernandez-Lamas, María del Carmen
Vydáno v Int J Mol Sci (2016)

Mechanism of Action and Clinical Application of Tafamidis in Hereditary Transthyretin Amyloidosis

Autor Coelho, Teresa, Merlini, Giampaolo, Bulawa, Christine E., Fleming, James A., Judge, Daniel P., Kelly, Jeffery W., Maurer, Mathew S., Planté-Bordeneuve, Violaine, Labaudinière, Richard, Mundayat, Rajiv, Riley, Steve, Lombardo, Ilise, Huertas, Pedro
Vydáno v Neurol Ther (2016)