Gait Analysis in a Mecp2 Knockout Mouse Model of Rett Syndrome Reveals Early-Onset and Progressive Motor Deficits

Por Gadalla, Kamal K. E., Ross, Paul D., Riddell, John S., Bailey, Mark E. S., Cobb, Stuart R.
Publicado no PLoS One (2014)

Development of a Novel AAV Gene Therapy Cassette with Improved Safety Features and Efficacy in a Mouse Model of Rett Syndrome

Por Gadalla, Kamal K.E., Vudhironarit, Thishnapha, Hector, Ralph D., Sinnett, Sarah, Bahey, Noha G., Bailey, Mark E.S., Gray, Steven J., Cobb, Stuart R.
Publicado no Mol Ther Methods Clin Dev (2017)

Improved MECP2 Gene Therapy Extends the Survival of MeCP2-Null Mice without Apparent Toxicity after Intracisternal Delivery

Por Sinnett, Sarah E., Hector, Ralph D., Gadalla, Kamal K.E., Heindel, Clifford, Chen, Daphne, Zaric, Violeta, Bailey, Mark E.S., Cobb, Stuart R., Gray, Steven J.
Publicado no Mol Ther Methods Clin Dev (2017)