Embryo-Based Large Fragment Knock-in in Mammals: Why, How and What’s Next

von Erwood, Steven, Gu, Bin
Veröffentlicht in Genes (Basel) (2020)

Activity of lumacaftor is not conserved in zebrafish Cftr bearing the major cystic fibrosis‐causing mutation

von Laselva, Onofrio, Erwood, Steven, Du, Kai, Ivakine, Zhenya, Bear, Christine E.
Veröffentlicht in FASEB Bioadv (2019)

STAT1 gain-of-function heterozygous cell models reveal diverse interferon-signature gene transcriptional responses

von Scott, Ori, Lindsay, Kyle, Erwood, Steven, Mollica, Antonio, Roifman, Chaim M., Cohn, Ronald D., Ivakine, Evgueni A.
Veröffentlicht in NPJ Genom Med (2021)

Modeling Niemann–Pick disease type C in a human haploid cell line allows for patient variant characterization and clinical interpretation

von Erwood, Steven, Brewer, Reid A., Bily, Teija M.I., Maino, Eleonora, Zhou, Liangchi, Cohn, Ronald D., Ivakine, Evgueni A.
Veröffentlicht in Genome Res (2019)

Allele-Specific Prevention of Nonsense-Mediated Decay in Cystic Fibrosis Using Homology-Independent Genome Editing

von Erwood, Steven, Laselva, Onofrio, Bily, Teija M.I., Brewer, Reid A., Rutherford, Alexandra H., Bear, Christine E., Ivakine, Evgueni A.
Veröffentlicht in Mol Ther Methods Clin Dev (2020)

Anti-CRISPR AcrIIA5 Potently Inhibits All Cas9 Homologs Used for Genome Editing

von Garcia, Bianca, Lee, Jooyoung, Edraki, Alireza, Hidalgo-Reyes, Yurima, Erwood, Steven, Mir, Aamir, Trost, Chantel N., Seroussi, Uri, Stanley, Sabrina Y., Cohn, Ronald D., Claycomb, Julie M., Sontheimer, Erik J., Maxwell, Karen L., Davidson, Alan R.
Veröffentlicht in Cell Rep (2019)