Differential Effects of DNA Double-Strand Break Repair Pathways on Single-Strand and Self-Complementary Adeno-Associated Virus Vector Genomes

Por Cataldi, Marcela P., McCarty, Douglas M.
Publicado em 2010

Hairpin end conformation of adeno-associated virus (AAV) genome determines interactions with DNA repair pathways

Por Cataldi, Marcela P., McCarty, Douglas M.
Publicado em 2012

Ribitol restores functionally glycosylated α-dystroglycan and improves muscle function in dystrophic FKRP-mutant mice

Por Cataldi, Marcela P., Lu, Peijuan, Blaeser, Anthony, Lu, Qi Long
Publicado no Nat Commun (2018)

Functional correction of neurological and somatic disorders at later stages of disease in MPS IIIA mice by systemic scAAV9-hSGSH gene delivery

Por Fu, Haiyan, Cataldi, Marcela P, Ware, Tierra A, Zaraspe, Kimberly, Meadows, Aaron S, Murrey, Darren A, McCarty, Douglas M
Publicado no Mol Ther Methods Clin Dev (2016)