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Utility of Huntington's Disease Assessments by Disease Stage: Floor/Ceiling Effects

Introduction: An understanding of the clinimetric properties of clinical assessments, including their constraints, is critical to sound clinical study and trial design. Utilizing data from Enroll-HD—a global, prospective HD observational study and clinical research platform—we examined several well-...

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Detalhes bibliográficos
Publicado no:Front Neurol
Main Authors: Abreu, Daisy, Ware, Jennifer, Georgiou-Karistianis, Nellie, Leavitt, Blair R., Fitzer-Attas, Cheryl J., Lobo, Raquel, Fernandes, Ana Raquel, Handley, Olivia, Anderson, Karen E., Stout, Julie C., Sampaio, Cristina
Formato: Artigo
Idioma:Inglês
Publicado em: Frontiers Media S.A. 2021
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC8320772/
https://ncbi.nlm.nih.gov/pubmed/34335433
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3389/fneur.2021.595679
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