Final results of the PUPs B-LONG study: evaluating safety and efficacy of rFIXFc in previously untreated patients with hemophilia B

PUPs B-LONG evaluated the safety and efficacy of recombinant factor IX Fc fusion protein (rFIXFc) in previously untreated patients (PUPs) with hemophilia B. In this open-label, phase 3 study, male PUPs (age <18 years) with hemophilia B (≤2 IU/dL of endogenous factor IX [FIX]) were to receive trea...

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Bibliographic Details
Published in:Blood Adv
Main Authors: Nolan, Beatrice, Klukowska, Anna, Shapiro, Amy, Rauch, Antoine, Recht, Michael, Ragni, Margaret, Curtin, Julie, Gunawardena, Sriya, Mukhopadhyay, Sutirtha, Jayawardene, Deepthi, Winding, Bent, Fischer, Kathelijn, Liesner, Raina
Format: Artigo
Language:Inglês
Published: American Society of Hematology 2021
Subjects:
Clinical Trials and Observations
Online Access:https://ncbi.nlm.nih.gov/pmc/articles/PMC8288672/
https://ncbi.nlm.nih.gov/pubmed/34242387
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1182/bloodadvances.2020004085
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