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Systemic antisense therapeutics inhibiting DUX4 expression ameliorates FSHD-like pathology in an FSHD mouse model

Aberrant expression of the double homeobox 4 (DUX4) gene in skeletal muscle causes muscle deterioration and weakness in Facioscapulohumeral muscular dystrophy (FSHD). Since the presence of a permissive pLAM1 polyadenylation signal is essential for stabilization of DUX4 mRNA and translation of DUX4 p...

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Bibliografiske detaljer
Udgivet i:Hum Mol Genet
Main Authors: Lu-Nguyen, Ngoc, Malerba, Alberto, Herath, Shan, Dickson, George, Popplewell, Linda
Format: Artigo
Sprog:Inglês
Udgivet: Oxford University Press 2021
Fag:
Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC8283208/
https://ncbi.nlm.nih.gov/pubmed/33987655
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddab136
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