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Case Report: Pansynostosis, Chiari I Malformation and Syringomyelia in a Child With Frontometaphyseal Dysplasia 1

Frontometaphyseal dysplasia 1 (FMD1) is a rare otopalatodigital spectrum disorder (OPDSD) that is inherited as an X-linked trait and it is caused by gain-of-function mutations in the FLNA. It is characterized by generalized skeletal dysplasia, and craniofacial abnormalities including facial dysmorph...

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Detalhes bibliográficos
Publicado no:Front Pediatr
Main Authors: Kim, Jaewon, Lee, Dong-Woo, Jang, Dae-Hyun
Formato: Artigo
Idioma:Inglês
Publicado em: Frontiers Media S.A. 2021
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC8280522/
https://ncbi.nlm.nih.gov/pubmed/34277511
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3389/fped.2021.574402
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