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The facioscapulohumeral muscular dystrophy Rasch‐built overall disability scale (FSHD‐RODS)

BACKGROUND AND OBJECTIVES: Facioscapulohumeral muscular dystrophy (FHSD) is a debilitating inherited muscle disease for which various therapeutic strategies are being investigated. Thus far, little attention has been given in FSHD to the development of scientifically sound outcome measures fulfillin...

Täydet tiedot

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Bibliografiset tiedot
Julkaisussa:Eur J Neurol
Päätekijät: Mul, Karlien, Hamadeh, Tatiana, Horlings, Corinne G. C., Tawil, Rabi, Statland, Jeffrey M., Sacconi, Sabrina, Corbett, Alastair J., Voermans, Nicol C., Faber, Catharina G., van Engelen, Baziel G. M., Merkies, Ingemar S. J.
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: John Wiley and Sons Inc. 2021
Aiheet:
Linkit:https://ncbi.nlm.nih.gov/pmc/articles/PMC8251612/
https://ncbi.nlm.nih.gov/pubmed/33838063
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1111/ene.14863
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