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The facioscapulohumeral muscular dystrophy Rasch‐built overall disability scale (FSHD‐RODS)

BACKGROUND AND OBJECTIVES: Facioscapulohumeral muscular dystrophy (FHSD) is a debilitating inherited muscle disease for which various therapeutic strategies are being investigated. Thus far, little attention has been given in FSHD to the development of scientifically sound outcome measures fulfillin...

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Bibliografski detalji
Izdano u:Eur J Neurol
Glavni autori: Mul, Karlien, Hamadeh, Tatiana, Horlings, Corinne G. C., Tawil, Rabi, Statland, Jeffrey M., Sacconi, Sabrina, Corbett, Alastair J., Voermans, Nicol C., Faber, Catharina G., van Engelen, Baziel G. M., Merkies, Ingemar S. J.
Format: Artigo
Jezik:Inglês
Izdano: John Wiley and Sons Inc. 2021
Teme:
Online pristup:https://ncbi.nlm.nih.gov/pmc/articles/PMC8251612/
https://ncbi.nlm.nih.gov/pubmed/33838063
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1111/ene.14863
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