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Neurodegeneration in Niemann–Pick Type C Disease: An Updated Review on Pharmacological and Non-Pharmacological Approaches to Counteract Brain and Cognitive Impairment

Niemann–Pick type C (NPC) disease is an autosomal recessive storage disorder, characterized by abnormal sequestration of unesterified cholesterol in the late endo-lysosomal system of cells. Progressive neurological deterioration and the onset of symptoms, such as ataxia, seizures, cognitive decline,...

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Dades bibliogràfiques
Publicat a:Int J Mol Sci
Autors principals: Cariati, Ida, Masuelli, Laura, Bei, Roberto, Tancredi, Virginia, Frank, Claudio, D’Arcangelo, Giovanna
Format: Artigo
Idioma:Inglês
Publicat: MDPI 2021
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC8234817/
https://ncbi.nlm.nih.gov/pubmed/34202978
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms22126600
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