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Cell and Gene Therapy for Anemia: Hematopoietic Stem Cells and Gene Editing

Hereditary anemia has various manifestations, such as sickle cell disease (SCD), Fanconi anemia, glucose-6-phosphate dehydrogenase deficiency (G6PDD), and thalassemia. The available management strategies for these disorders are still unsatisfactory and do not eliminate the main causes. As genetic ab...

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Detalhes bibliográficos
Publicado no:Int J Mol Sci
Main Authors: Anurogo, Dito, Yuli Prasetyo Budi, Nova, Thi Ngo, Mai-Huong, Huang, Yen-Hua, Pawitan, Jeanne Adiwinata
Formato: Artigo
Idioma:Inglês
Publicado em: MDPI 2021
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC8230702/
https://ncbi.nlm.nih.gov/pubmed/34200975
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms22126275
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