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Survival of patients with rare diseases: a population-based study in Tuscany (Italy)

BACKGROUND: Rare diseases (RDs) encompass a heterogeneous group of life-threatening or chronically debilitating conditions that individually affect a small number of subjects but overall represent a major public health issue globally. There are still limited data on RD burden due to the paucity of l...

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Dades bibliogràfiques
Publicat a:Orphanet J Rare Dis
Autors principals: Gorini, Francesca, Coi, Alessio, Mezzasalma, Lorena, Baldacci, Silvia, Pierini, Anna, Santoro, Michele
Format: Artigo
Idioma:Inglês
Publicat: BioMed Central 2021
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC8201697/
https://ncbi.nlm.nih.gov/pubmed/34127030
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-021-01907-0
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