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Dynamic treatment regimens in small n, sequential, multiple assignment, randomized trials: An application in focal segmental glomerulosclerosis

Focal segmental glomerulosclerosis (FSGS) is a rare kidney disease with an annual incidence of 0.2–1.8 cases per 100,000 individuals. Most rare diseases like FSGS lack effective treatments, and it is difficult to implement clinical trials to study rare diseases because of the small sample sizes and...

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Publicado en:Contemp Clin Trials
Main Authors: Chao, Yan-Cheng, Trachtman, Howard, Gipson, Debbie S., Spino, Cathie, Braun, Thomas M., Kidwell, Kelley M.
Formato: Artigo
Idioma:Inglês
Publicado: 2020
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC8173713/
https://ncbi.nlm.nih.gov/pubmed/32200006
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.cct.2020.105989
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