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Stepwise shortening of agalsidase beta infusion duration in Fabry disease: Clinical experience with infusion rate escalation protocol

BACKGROUND: Although enzyme replacement therapy with agalsidase beta resulted in a variety of clinical benefits, life‐long biweekly intravenous infusion may impact on patients’ quality of life. Moreover, regular infusions are time‐consuming: although a stepwise shortening of infusion duration is all...

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Detalhes bibliográficos
Publicado no:Mol Genet Genomic Med
Main Authors: Riccio, Eleonora, Zanfardino, Mario, Franzese, Monica, Capuano, Ivana, Buonanno, Pasquale, Ferreri, Lucia, Amicone, Maria, Pisani, Antonio
Formato: Artigo
Idioma:Inglês
Publicado em: John Wiley and Sons Inc. 2021
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC8172210/
https://ncbi.nlm.nih.gov/pubmed/33755336
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/mgg3.1659
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