Loading...
Adeno-associated virus gene therapy to the rescue for Charcot-Marie-Tooth disease type 4J
The genetic peripheral neuropathy known as Charcot-Marie-Tooth disease type 4J (CMT4J) is caused by recessive mutations in the FIG4 gene. The transformational success of adeno-associated virus (AAV) gene therapy for spinal muscular atrophy has generated substantial interest in using this approach to...
Na minha lista:
| Udgivet i: | J Clin Invest |
|---|---|
| Hovedforfatter: | |
| Format: | Artigo |
| Sprog: | Inglês |
| Udgivet: |
American Society for Clinical Investigation
2021
|
| Fag: | |
| Online adgang: | https://ncbi.nlm.nih.gov/pmc/articles/PMC8159695/ https://ncbi.nlm.nih.gov/pubmed/34060476 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1172/JCI149492 |
| Tags: |
Tilføj Tag
Ingen Tags, Vær først til at tagge denne postø!
|