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Identification and Classification of Rare Variants in NPC1 and NPC2 in Quebec

Niemann–Pick disease type C (NPC) is a treatable autosomal recessive neurodegenerative condition which leads to a variety of progressive manifestations. Despite most cases being diagnosed at a young age, disease prevalence may be underestimated, especially in adults, and interpretation of NPC1 and N...

Täydet tiedot

Tallennettuna:
Bibliografiset tiedot
Julkaisussa:Sci Rep
Päätekijät: Touma, Lahoud, Labrecque, Marjorie, Tetreault, Martine, Duquette, Antoine
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: Nature Publishing Group UK 2021
Aiheet:
Linkit:https://ncbi.nlm.nih.gov/pmc/articles/PMC8121778/
https://ncbi.nlm.nih.gov/pubmed/33990640
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41598-021-89630-5
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