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Novel treatment options for acute hepatic porphyrias

PURPOSE OF REVIEW: Acute hepatic porphyrias (AHP) are a group of rare diseases that are characterized by episodic acute neurovisceral pain episodes caused by abnormal accumulation of the neurotoxic porphyrin precursor delta-aminolevulinic acid (ALA). Patient with frequent recurrent acute attacks hav...

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Dades bibliogràfiques
Publicat a:Curr Opin Gastroenterol
Autor principal: Wang, Bruce
Format: Artigo
Idioma:Inglês
Publicat: 2021
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC8104969/
https://ncbi.nlm.nih.gov/pubmed/33769375
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1097/MOG.0000000000000734
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