A carregar...

Gene Therapy for Lysosomal Storage Disorders: Ongoing Studies and Clinical Development

Rare monogenic disorders such as lysosomal diseases have been at the forefront in the development of novel treatments where therapeutic options are either limited or unavailable. The increasing number of successful pre-clinical and clinical studies in the last decade demonstrates that gene therapy r...

ver descrição completa

Na minha lista:
Detalhes bibliográficos
Publicado no:Biomolecules
Main Authors: Massaro, Giulia, Geard, Amy F., Liu, Wenfei, Coombe-Tennant, Oliver, Waddington, Simon N., Baruteau, Julien, Gissen, Paul, Rahim, Ahad A.
Formato: Artigo
Idioma:Inglês
Publicado em: MDPI 2021
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC8074255/
https://ncbi.nlm.nih.gov/pubmed/33924076
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/biom11040611
Tags: Adicionar Tag
Sem tags, seja o primeiro a adicionar uma tag!