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Real-World Outcomes of Ivacaftor Treatment in People with Cystic Fibrosis: A Systematic Review

Cystic fibrosis (CF) is a rare, progressive, multi-organ genetic disease. Ivacaftor, a small-molecule CF transmembrane conductance regulator modulator, was the first medication to treat the underlying cause of CF. Since its approval, real-world clinical experience on the use of ivacaftor has been do...

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Библиографические подробности
Опубликовано в: :J Clin Med
Главные авторы: Duckers, Jamie, Lesher, Beth, Thorat, Teja, Lucas, Eleanor, McGarry, Lisa J., Chandarana, Keval, De Iorio, Fosca
Формат: Artigo
Язык:Inglês
Опубликовано: MDPI 2021
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC8038673/
https://ncbi.nlm.nih.gov/pubmed/33917386
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/jcm10071527
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