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Nusinersen Wearing-Off in Adult 5q-Spinal Muscular Atrophy Patients

The antisense oligonucleotide nusinersen was the first drug treatment available for all types of 5q-spinal muscular atrophy (SMA). The dosing regime has been derived from pivotal clinical trials in infants and children. The efficacy of nusinersen in severely affected adult SMA patients is still ques...

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Detalhes bibliográficos
Publicado no:Brain Sci
Main Authors: Osmanovic, Alma, Schreiber-Katz, Olivia, Petri, Susanne
Formato: Artigo
Idioma:Inglês
Publicado em: MDPI 2021
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7998943/
https://ncbi.nlm.nih.gov/pubmed/33805645
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/brainsci11030367
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