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Clinical, humanistic, and economic burden of severe hemophilia B in the United States: Results from the CHESS US and CHESS US+ population surveys

BACKGROUND: Hemophilia B is a rare congenital bleeding disorder that has a significant negative impact on patients’ functionality and health-related quality of life. The standard of care for severe hemophilia B in the United States is prophylactic factor IX replacement therapy, which incurs substant...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Orphanet J Rare Dis
Egile Nagusiak: Burke, Tom, Asghar, Sohaib, O’Hara, Jamie, Sawyer, Eileen K., Li, Nanxin
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: BioMed Central 2021
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC7981988/
https://ncbi.nlm.nih.gov/pubmed/33743752
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-021-01774-9
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