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Novel GLA T194A variant causes Fabry disease

Fabry disease (FD) is an X-linked, systemic lysosomal deposition disease caused by alpha-galactosidase A (AGAL) enzyme deficiency deriving out of changes on the GLA gene. Though several mutations have been described, one must consider that even a specific mutation may present with variable clinical...

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Detalhes bibliográficos
Publicado no:BMJ Case Rep
Main Authors: Pestana, Maria Nicole, Gomes da Silva, Francisca, Durães, José, Silva, Gil
Formato: Artigo
Idioma:Inglês
Publicado em: BMJ Publishing Group 2021
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7929876/
https://ncbi.nlm.nih.gov/pubmed/33649041
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1136/bcr-2020-239204
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