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Primary Ciliary Dyskinesia Diagnostic Challenges: Understanding the Clinical Phenotype of the Puerto Rican RSPH4A Founder Mutation

Primary ciliary dyskinesia (PCD) is a rare, heterogeneous ciliopathy resulting in chronic oto-sino-pulmonary disease, bronchiectasis, newborn respiratory distress, and laterality defects. PCD diagnosis can be achieved by following diagnostic algorithms that include electron microscopy, genetics, and...

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Detalhes bibliográficos
Publicado no:Diagnostics (Basel)
Main Authors: De Jesús-Rojas, Wilfredo, Reyes-De Jesús, Dalilah, Mosquera, Ricardo A.
Formato: Artigo
Idioma:Inglês
Publicado em: MDPI 2021
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7918725/
https://ncbi.nlm.nih.gov/pubmed/33670432
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/diagnostics11020281
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