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An observational cohort study on impact, dimensions and outcome of perceived fatigue in adult 5q-spinal muscular atrophy patients receiving nusinersen treatment

BACKGROUND: Efficacy of nusinersen in adult 5q-spinal muscular atrophy (SMA) patients regarding motor function has recently been demonstrated. However, additional outcome measures are needed to capture non-motor improvements. Fatigue is a common and disabling symptom in neurologic diseases, but litt...

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Détails bibliographiques
Publié dans:J Neurol
Auteurs principaux: Binz, Camilla, Schreiber-Katz, Olivia, Kumpe, Mareike, Ranxha, Gresa, Siegler, Hannah, Wieselmann, Gary, Petri, Susanne, Osmanovic, Alma
Format: Artigo
Langue:Inglês
Publié: Springer Berlin Heidelberg 2020
Sujets:
Accès en ligne:https://ncbi.nlm.nih.gov/pmc/articles/PMC7914247/
https://ncbi.nlm.nih.gov/pubmed/33029682
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s00415-020-10227-5
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