Do we always need to treat patients with spinal muscular atrophy? A personal view and experience

BACKGROUND: We report the clinical outcomes observed in our patients with SMA type 1 or 2 receiving nusinersen, and we comment on the ethical implications of this treatment, in line with our results and those reported by Audic et al. in their analysis published in the Orphanet Journal of Rare Diseas...

Popoln opis

Shranjeno v:
Bibliografske podrobnosti
izdano v:Orphanet J Rare Dis
Main Authors: Agosto, Caterina, Salamon, Eleonora, Divisic, Antuan, Benedetti, Francesca, Giacomelli, Luca, Shah, Aashni, Perilongo, Giorgio, Benini, Franca
Format: Artigo
Jezik:Inglês
Izdano: BioMed Central 2021
Teme:
Letter to the Editor
Online dostop:https://ncbi.nlm.nih.gov/pmc/articles/PMC7879688/
https://ncbi.nlm.nih.gov/pubmed/33573692
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-020-01593-4
Oznake: Označite
Brez oznak, prvi označite!

Podobne knjige/članki