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Patient-reported burden of hereditary transthyretin amyloidosis on functioning and well-being
BACKGROUND: Hereditary transthyretin (hATTR) amyloidosis is a rare, systemic, progressive, and life-threatening disease in which transthyretin proteins misfold and aggregate as insoluble amyloid deposits, disrupting nervous, cardiac, gastrointestinal, and other organ tissues. There are limited avail...
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| Publicado no: | J Patient Rep Outcomes |
|---|---|
| Main Authors: | , , , , , |
| Formato: | Artigo |
| Idioma: | Inglês |
| Publicado em: |
Springer International Publishing
2021
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| Assuntos: | |
| Acesso em linha: | https://ncbi.nlm.nih.gov/pmc/articles/PMC7790957/ https://ncbi.nlm.nih.gov/pubmed/33411323 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s41687-020-00273-y |
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