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Patient-reported burden of hereditary transthyretin amyloidosis on functioning and well-being

BACKGROUND: Hereditary transthyretin (hATTR) amyloidosis is a rare, systemic, progressive, and life-threatening disease in which transthyretin proteins misfold and aggregate as insoluble amyloid deposits, disrupting nervous, cardiac, gastrointestinal, and other organ tissues. There are limited avail...

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Dades bibliogràfiques
Publicat a:J Patient Rep Outcomes
Autors principals: Lovley, Andrew, Raymond, Kimberly, Guthrie, Spencer D., Pollock, Michael, Sanchorawala, Vaishali, White, Michelle K.
Format: Artigo
Idioma:Inglês
Publicat: Springer International Publishing 2021
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC7790957/
https://ncbi.nlm.nih.gov/pubmed/33411323
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s41687-020-00273-y
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