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Advances in Treatment of ATTRv Amyloidosis: State of the Art and Future Prospects

Hereditary amyloid transthyretin (ATTRv) amyloidosis with polyneuropathy is a progressive disease that is transmitted as an autosomal dominant trait and characterized by multiple organ failure, including axonal sensory-motor neuropathy, cardiac involvement, and autonomic dysfunction. Liver transplan...

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Библиографические подробности
Опубликовано в: :Brain Sci
Главные авторы: Russo, Massimo, Gentile, Luca, Toscano, Antonio, Aguennouz, M’Hammed, Vita, Giuseppe, Mazzeo, Anna
Формат: Artigo
Язык:Inglês
Опубликовано: MDPI 2020
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC7763612/
https://ncbi.nlm.nih.gov/pubmed/33316911
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/brainsci10120952
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