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Novel ACADVL variants resulting in mitochondrial defects in long-chain acyl-CoA dehydrogenase deficiency

The pathogenesis of very-long-chain acyl-CoA dehydrogenase (VLCAD) deficiency is highly heterogeneous and still unclear. Additional novel variants have been recently detected in the population. The molecular and cellular effects of these previously unreported variants are still poorly understood and...

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Dettagli Bibliografici
Pubblicato in:J Zhejiang Univ Sci B
Autori principali: Chen, Ting, Tong, Fan, Wu, Xiao-yu, Zhu, Ling, Yi, Qiu-zi, Zheng, Jing, Yang, Ru-lai, Zhao, Zheng-yan, Cang, Xiao-hui, Shu, Qiang, Jiang, Ping-ping
Natura: Artigo
Lingua:Inglês
Pubblicazione: Zhejiang University Press 2020
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7691688/
https://ncbi.nlm.nih.gov/pubmed/33150772
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1631/jzus.B2000339
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