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Two novel mutations in the DNAH11 gene in primary ciliary dyskinesia (CILD7) with considerable variety in the clinical and beating cilia phenotype

BACKGROUND: Diagnosis of primary ciliary dyskinesia (PCD) still remains a challenge, especially with mutations in the Dynein Arm Heavy Chain 11 (DNAH11) gene. Classical diagnostic measures like Transmission Electron Microscopy (TEM) are not applicable for mutations in the DNAH11 gene since ultrastru...

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Pubblicato in:BMC Med Genet
Autori principali: Schultz, Rüdiger, Elenius, Varpu, Lukkarinen, Heikki, Saarela, Tanja
Natura: Artigo
Lingua:Inglês
Pubblicazione: BioMed Central 2020
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7690114/
https://ncbi.nlm.nih.gov/pubmed/33243178
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s12881-020-01171-2
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