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Hearing loss in patients with mucopolysaccharidoses‐1 and ‐6 after hematopoietic cell transplantation: A longitudinal analysis

Hearing loss is frequently seen in mucopolysaccharidoses (MPS) patients. Although hematopoietic cell transplantation (HCT) increases overall survival, disease progression is observed in certain tissues. This study describes the course of hearing loss (HL) over time in transplanted MPS patients. Tran...

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Publicado en:J Inherit Metab Dis
Autores principales: van den Broek, Brigitte T. A., Smit, Adriana L., Boelens, Jaap Jan, van Hasselt, Peter M.
Formato: Artigo
Lenguaje:Inglês
Publicado: John Wiley & Sons, Inc. 2020
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC7689745/
https://ncbi.nlm.nih.gov/pubmed/32579781
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/jimd.12277
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