Cost-Effectiveness of Nusinersen and Universal Newborn Screening for Spinal Muscular Atrophy

OBJECTIVE: To evaluate the cost-effectiveness of nusinersen with and without universal newborn screening for infantile-onset spinal muscular atrophy (SMA). STUDY DESIGN: Markov model using data from clinical trials with U.S. epidemiologic and cost data was developed. Primary interventions studied we...

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Bibliografske podrobnosti
izdano v:J Pediatr
Main Authors: Jalali, Ali, Rothwell, Erin, Botkin, Jeffrey R., Anderson, Rebecca A., Butterfield, Russell J, Nelson, Richard E.
Format: Artigo
Jezik:Inglês
Izdano: 2020
Teme:
Article
Online dostop:https://ncbi.nlm.nih.gov/pmc/articles/PMC7686158/
https://ncbi.nlm.nih.gov/pubmed/32659229
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.jpeds.2020.07.033
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