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Ultrastructural and diffusion tensor imaging studies reveal axon abnormalities in Pompe disease mice

Pompe disease (PD) is caused by lysosomal glycogen accumulation in tissues, including muscles and the central nervous system (CNS). The intravenous infusion of recombinant human acid alpha-glucosidase (rhGAA) rescues the muscle pathologies in PD but does not treat the CNS because rhGAA does not cros...

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Dettagli Bibliografici
Pubblicato in:Sci Rep
Autori principali: Lee, Ni-Chung, Peng, Wei-Hao, Tsai, Li-Kai, Lu, Yen-Hsu, Wang, Hao-Chun, Shih, Yao-Chia, Pung, Zeng-Xian, Hu, Hsi-Yuan, Hwu, Wuh-Liang, Tseng, Wen-Yih Isaac, Chien, Yin-Hsiu
Natura: Artigo
Lingua:Inglês
Pubblicazione: Nature Publishing Group UK 2020
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7677380/
https://ncbi.nlm.nih.gov/pubmed/33214573
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41598-020-77193-w
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