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De novo variants in WDR45 underlie beta‐propeller protein‐associated neurodegeneration in five independent families

BACKGROUND: Beta‐propeller protein‐associated neurodegeneration (BPAN) is a rare, X‐linked dominant neurodegenerative disease mainly characterized by developmental delay, intellectual disability, epilepsy in childhood and dystonia, parkinsonism, dementia in adulthood. BPAN is caused by variants in W...

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Detalhes bibliográficos
Publicado no:Mol Genet Genomic Med
Main Authors: Tang, Xiaojun, Lan, Xiaoping, Song, Xiaozhen, Xu, Wuhen, Zhang, Yuanfeng, Zhang, Hong, Wu, Shengnan
Formato: Artigo
Idioma:Inglês
Publicado em: John Wiley and Sons Inc. 2020
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7667327/
https://ncbi.nlm.nih.gov/pubmed/33037762
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/mgg3.1499
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