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Integrating Data From Randomized Controlled Trials and Observational Studies to Assess Survival in Rare Diseases: Insights From Pulmonary Arterial Hypertension

BACKGROUND: Conducting randomized controlled trials to investigate survival in a rare disease like pulmonary arterial hypertension has considerable ethical and logistical constraints. In many studies, such as the Study with an Endothelin Receptor Antagonist in Pulmonary Arterial Hypertension to Impr...

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Bibliografiske detaljer
Udgivet i:Circ Cardiovasc Qual Outcomes
Main Authors: Torbicki, Adam, Bacchi, Marisa, Delcroix, Marion, Farber, Harrison W., Ghofrani, Hossein-Ardeschir, Hennessy, Brian, Jansa, Pavel, Mehta, Sanjay, Perchenet, Loïc, Pulido, Tomas, Rosenberg, Daniel, Rubin, Lewis J., Sastry, B.K.S., Simonneau, Gérald, Sitbon, Olivier, Souza, Rogério, Wei, Lee-Jen, Channick, Richard, Benza, Raymond
Format: Artigo
Sprog:Inglês
Udgivet: Lippincott Williams & Wilkins 2019
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Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC7665498/
https://ncbi.nlm.nih.gov/pubmed/31109190
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1161/CIRCOUTCOMES.118.005095
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