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The Cerebellum in Niemann-Pick C1 Disease: Mouse Versus Man

Selective neuronal vulnerability is common to most degenerative disorders, including Niemann-Pick C (NPC), a rare genetic disease with altered intracellular trafficking of cholesterol. Purkinje cell dysfunction and loss are responsible for cerebellar ataxia, which is among the prevailing neurologica...

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Detalhes bibliográficos
Publicado no:Cerebellum
Main Authors: Fiorenza, Maria Teresa, La Rosa, Piergiorgio, Canterini, Sonia, Erickson, Robert P.
Formato: Artigo
Idioma:Inglês
Publicado em: 2023
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7617266/
https://ncbi.nlm.nih.gov/pubmed/35040097
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s12311-021-01347-3
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