Chargement en cours...

Long Term Follow-Up of Polish Patients with Isovaleric Aciduria. Clinical and Molecular Delineation of Isovaleric Aciduria

Isovaleric acidemia (IVA) is an autosomal recessive leucine inborn error of metabolism caused by isovaleryl-CoA dehydrogenase deficiency. The disease has various courses, from severe ones manifesting in newborns to the intermittent form with first manifestation in children and adults. The aim of thi...

Description complète

Enregistré dans:
Détails bibliographiques
Publié dans:Diagnostics (Basel)
Auteurs principaux: Szymańska, Edyta, Jezela-Stanek, Aleksandra, Bogdańska, Anna, Rokicki, Dariusz, Ehmke vel Emczyńska-Seliga, Ewa, Pajdowska, Magdalena, Ciara, Elżbieta, Tylki-Szymańska, Anna
Format: Artigo
Langue:Inglês
Publié: MDPI 2020
Sujets:
Accès en ligne:https://ncbi.nlm.nih.gov/pmc/articles/PMC7598207/
https://ncbi.nlm.nih.gov/pubmed/32977617
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/diagnostics10100738
Tags: Ajouter un tag
Pas de tags, Soyez le premier à ajouter un tag!