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Preclinical evaluation of a next-generation, subcutaneously administered, coagulation factor IX variant, dalcinonacog alfa

INTRODUCTION: The rapid clearance of factor IX necessitates frequent intravenous administrations to achieve effective prophylaxis for patients with hemophilia B. Subcutaneous administration has historically been limited by low bioavailability and potency. Dalcinonacog alfa was developed using a rati...

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Détails bibliographiques
Publié dans:PLoS One
Auteurs principaux: Nichols, Timothy C., Levy, Howard, Merricks, Elizabeth P., Raymer, Robin A., Lee, Martin L.
Format: Artigo
Langue:Inglês
Publié: Public Library of Science 2020
Sujets:
Accès en ligne:https://ncbi.nlm.nih.gov/pmc/articles/PMC7592742/
https://ncbi.nlm.nih.gov/pubmed/33112889
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1371/journal.pone.0240896
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