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Therapeutic strategies for acute intermittent porphyria

Acute intermittent porphyria (AIP) is an autosomal dominant disease caused by mutations in porphobilinogen deaminase (PBGD), the third enzyme of the heme synthesis pathway. Symptoms of AIP usually manifest as intermittent acute attacks with occasional neuropsychiatric crises. The management of AIP i...

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Détails bibliographiques
Publié dans:Intractable Rare Dis Res
Auteurs principaux: Zhao, Lanlan, Wang, Xinyang, Zhang, Xiaoning, Liu, Xiantao, Ma, Ningzhen, Zhang, Yiran, Zhang, Songyun
Format: Artigo
Langue:Inglês
Publié: International Research and Cooperation Association for Bio & Socio-Sciences Advancement 2020
Sujets:
Accès en ligne:https://ncbi.nlm.nih.gov/pmc/articles/PMC7586882/
https://ncbi.nlm.nih.gov/pubmed/33139979
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.5582/irdr.2020.03089
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