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Triheptanoin: First Approval

Triheptanoin (Dojolvi™), a synthetic medium-chain triglyceride, is being developed by Ultragenyx Pharmaceutical as a pharmaceutical-grade anaplerotic compound for use in the treatment of inherited metabolic disorders. In June 2020, triheptanoin received its first regulatory approval, in the USA, for...

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Detalles Bibliográficos
Publicado en:Drugs
Autor Principal: Shirley, Matt
Formato: Artigo
Idioma:Inglês
Publicado: Springer International Publishing 2020
Assuntos:
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC7575481/
https://ncbi.nlm.nih.gov/pubmed/32897506
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s40265-020-01399-5
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