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In Vivo Electroporation-Mediated, Intrahepatic Alpha1 Antitrypsin Gene Transfer Reduces Pulmonary Emphysema in Pallid Mice

Rationale: Mutation in the alpha1 antitrypsin (AAT) gene leads to low circulating levels of AAT, which is associated with several disease processes including pulmonary emphysema. The standard of care relies on substitution with plasma-purified AAT. We studied a novel approach to obtain sustained the...

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Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Pharmaceutics
Egile Nagusiak: Sutter, Marco A., Cremona, Tiziana P., Nita, Izabela, Cavarra, Eleonora, Lungarella, Giuseppe, Lewis, Eli C., Schittny, Johannes C., Geiser, Thomas, Gazdhar, Amiq
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: MDPI 2020
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC7559762/
https://ncbi.nlm.nih.gov/pubmed/32825773
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/pharmaceutics12090793
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